Gene Therapy Resources
It's an exciting time for gene therapy and the clinical research currently being conducted. And while there’s a lot of information out there about genetics and gene therapy, not all of it is clear and some may be incorrect or misleading.
The resources on this site are for patient advocacy groups only. If you have any questions or would like to request materials that are editable, please contact your local BioMarin representative or reach out to BioMarin.
Below, you'll find educational resources intended to help people better understand the science behind gene therapy research.
Gene Therapy Education Newsletters
A series of 6 educational newsletters designed to explain everything from what a gene is to what you might expect from gene therapy research.
Newsletter Vol 1
Newsletter Vol 2
Newsletter Vol 3
Newsletter Vol 4
Newsletter Vol 5
Newsletter Vol 6
Gene Therapy Brochure
A quick guide to the science behind gene therapy research.
A quick guide to the science behind gene therapy research.
Gene Therapy Lexicon Brochure
A brochure that details research with patients and healthcare professionals to determine the best language to use in educational materials.
A brochure that details research with patients and healthcare professionals to determine the best language to use in educational materials.
Gene Therapy Frequently Asked Questions
Have a question about gene therapy? We have answers.
Have a question about gene therapy? We have answers.
Gene Therapy Digital Image Library
A collection of images we use to help visually explain the science behind gene therapy.
A collection of images we use to help visually explain the science behind gene therapy.